{"id":26601,"date":"2023-03-02T10:34:57","date_gmt":"2023-03-02T13:34:57","guid":{"rendered":"https:\/\/mindthegraph.com\/blog\/understanding-cervical-cancer-copy\/"},"modified":"2023-03-09T17:59:22","modified_gmt":"2023-03-09T20:59:22","slug":"crispr-therapy","status":"publish","type":"post","link":"https:\/\/mindthegraph.com\/blog\/sk\/crispr-terapia\/","title":{"rendered":"Ako funguje terapia CRISPR v g\u00e9novej terapii?"},"content":{"rendered":"<p>Rakovina je u\u017e dlho zlo\u017eit\u00e9 a r\u00f4znorod\u00e9 ochorenie sp\u00f4soben\u00e9 zmenami v DNA jedinca, ktor\u00e9 aktivuj\u00fa onkog\u00e9ny a z\u00e1rove\u0148 inaktivuj\u00fa n\u00e1dorov\u00e9 supresory, \u010do sp\u00f4sobuje aj dysregul\u00e1ciu epigen\u00f3mu, ktor\u00fd m\u00e1 na starosti koordin\u00e1ciu norm\u00e1lnej expresie g\u00e9nov.<\/p>\n\n\n\n<p>Ak to zhrnieme, rakovina je ochorenie buniek, ktor\u00e9 sp\u00f4sobuje zmeny v metabolizme a \u0161trukt\u00fare buniek, \u010d\u00edm sa tieto bunky po\u0161kodia do takej miery, \u017ee u\u017e nefunguj\u00fa spr\u00e1vne a vyh\u00fdbaj\u00fa sa obrann\u00fdm mechanizmom hostite\u013ea.&nbsp;<\/p>\n\n\n\n<p>Ve\u013ek\u00e9 mno\u017estvo odborn\u00edkov a profesion\u00e1lov sa venuje sk\u00famaniu rakoviny, aby \u00faplne pochopili v\u0161etky jej zlo\u017eitosti a nejasnosti. Poznanie toho, ako sa men\u00ed gen\u00f3m, ako sa bunka prisp\u00f4sobuje a ako doch\u00e1dza k inici\u00e1cii ochorenia, je jedn\u00fdm z rozhoduj\u00facich faktorov pre v\u00fdvoj \u00fa\u010dinnej\u0161\u00edch mo\u017enost\u00ed lie\u010dby a zlep\u0161enie v\u00fdsledkov pre pacientov s rakovinou.&nbsp;<\/p>\n\n\n\n<p>Terapia CRISPR sa presadila ako technika na sk\u00famanie funkcie buniek a v\u00fdrazne ovplyvnila v\u00fdskum rakoviny, \u010do viedlo k nov\u00fdm poznatkom, ktor\u00e9 by mali ur\u00fdchli\u0165 diagnostiku a lie\u010dbu.&nbsp;<\/p>\n\n\n\n<h2>\u010co je terapia CRISPR?<\/h2>\n\n\n\n<p>Odkedy vedci zistili, \u017ee zmeny v DNA sp\u00f4sobuj\u00fa rakovinu, h\u013eadali sp\u00f4sob, ako tieto zmeny napravi\u0165 pomocou manipul\u00e1cie s DNA. Jedn\u00fdm z n\u00e1jden\u00fdch pr\u00edstupov je terapia CRISPR.<\/p>\n\n\n\n<p>Lie\u010dba CRISPR dok\u00e1\u017ee upravova\u0165 DNA \u013eudsk\u00fdch buniek rovnako ako mimoriadne presn\u00e9 a \u013eahko ovl\u00e1date\u013en\u00e9 no\u017enice. CRISPR upravuje g\u00e9ny tak, \u017ee opatrne strih\u00e1 DNA a potom systematicky umo\u017e\u0148uje jej opravu.&nbsp;<\/p>\n\n\n\n<div style=\"height:18px\" aria-hidden=\"true\" class=\"wp-block-spacer\"><\/div>\n\n\n<div class=\"wp-block-image\">\n<figure class=\"aligncenter size-full\"><img decoding=\"async\" loading=\"lazy\" width=\"651\" height=\"174\" src=\"https:\/\/mindthegraph.com\/blog\/wp-content\/uploads\/2023\/02\/banner-blog-trial-03.jpg\" alt=\"\" class=\"wp-image-26762\" srcset=\"https:\/\/mindthegraph.com\/blog\/wp-content\/uploads\/2023\/02\/banner-blog-trial-03.jpg 651w, https:\/\/mindthegraph.com\/blog\/wp-content\/uploads\/2023\/02\/banner-blog-trial-03-300x80.jpg 300w, https:\/\/mindthegraph.com\/blog\/wp-content\/uploads\/2023\/02\/banner-blog-trial-03-18x5.jpg 18w, https:\/\/mindthegraph.com\/blog\/wp-content\/uploads\/2023\/02\/banner-blog-trial-03-100x27.jpg 100w\" sizes=\"(max-width: 651px) 100vw, 651px\" \/><\/figure><\/div>\n\n\n<div style=\"height:18px\" aria-hidden=\"true\" class=\"wp-block-spacer\"><\/div>\n\n\n\n<h2>Ako funguje terapia CRISPR?<\/h2>\n\n\n\n<p>Technika CRISPR v laborat\u00f3riu zah\u0155\u0148a dve k\u013e\u00fa\u010dov\u00e9 postavy: vodiacu RNA a enz\u00fdm na rezanie DNA, naj\u010dastej\u0161ie Cas9.<\/p>\n\n\n\n<p>Ak chcete pou\u017ei\u0165 genetick\u00e9 no\u017enice CRISPR na zmenu gen\u00f3mu, mus\u00edte najprv n\u00e1js\u0165 sekvenciu DNA, ktor\u00e1 sa m\u00e1 zmeni\u0165. Po identifik\u00e1cii pr\u00edslu\u0161nej sekvencie DNA sa m\u00e1 rozpozna\u0165 a pripoji\u0165 k nej jedna vodiaca RNA (sgRNA).&nbsp;<\/p>\n\n\n\n<p>Sekvencia vodiacej RNA dop\u013a\u0148a sekvenciu cie\u013eovej DNA. To znamen\u00e1, \u017ee vodiaca RNA sa v ide\u00e1lnom pr\u00edpade pripoj\u00ed len k cie\u013eovej sekvencii DNA a nepripoj\u00ed sa k in\u00fdm \u010dastiam gen\u00f3mu.&nbsp;<\/p>\n\n\n\n<p>Enz\u00fdm Cas9 (prote\u00edn molekul\u00e1rnych no\u017en\u00edc) sa pripoj\u00ed k RNA a navedie no\u017enice na presn\u00e9 miesto v gen\u00f3me, kde je potrebn\u00e9 vykona\u0165 rez.&nbsp;<\/p>\n\n\n\n<p>Tento proces opravy m\u00f4\u017ee by\u0165 riaden\u00fd tak, aby modifikoval DNA v danom mieste gen\u00f3mu. Napr\u00edklad g\u00e9n sa m\u00f4\u017ee odstr\u00e1ni\u0165 alebo aktualizova\u0165, aby sa opravili v\u0161etky chyby v jeho sekvencii.<\/p>\n\n\n\n<p>V z\u00e1vislosti od toho, ako je syst\u00e9m CRISPR naprogramovan\u00fd, existuj\u00fa tri mo\u017en\u00e9 v\u00fdsledky, ke\u010f sa cie\u013eov\u00e1 sekvencia prere\u017ee:&nbsp;<\/p>\n\n\n\n<ol>\n<li>Na zacelenie rezu sa do DNA zavedie mut\u00e1cia.&nbsp;<\/li>\n\n\n\n<li>Enz\u00fdmy s\u00fa navrhnut\u00e9 tak, aby vytv\u00e1rali rezy na oboch stran\u00e1ch cie\u013eovej DNA s cie\u013eom odstr\u00e1ni\u0165 cie\u013eov\u00fa DNA a znovu spoji\u0165 konce.&nbsp;<\/li>\n\n\n\n<li>Segment HDR m\u00f4\u017ee by\u0165 vlo\u017een\u00fd do gen\u00f3mu homologickou rekombin\u00e1ciou.<a href=\"https:\/\/www.researchgate.net\/profile\/Konda-Mani-Saravanan\/publication\/355845141\/figure\/fig3\/AS:1128285891235840@1646015727249\/Mechanism-of-action-of-CRISPR-Cas9-techniques-CRIPSPR-Cas9-gene-with-cleavage-activities.png\"><\/a><\/li>\n<\/ol>\n\n\n\n<div style=\"height:18px\" aria-hidden=\"true\" class=\"wp-block-spacer\"><\/div>\n\n\n\n<figure class=\"wp-block-image size-large\"><img decoding=\"async\" loading=\"lazy\" width=\"1024\" height=\"896\" src=\"https:\/\/mindthegraph.com\/blog\/wp-content\/uploads\/2023\/02\/crispr-cas9-gene-editing-1024x896.jpg\" alt=\"\" class=\"wp-image-27027\" srcset=\"https:\/\/mindthegraph.com\/blog\/wp-content\/uploads\/2023\/02\/crispr-cas9-gene-editing-1024x896.jpg 1024w, https:\/\/mindthegraph.com\/blog\/wp-content\/uploads\/2023\/02\/crispr-cas9-gene-editing-300x263.jpg 300w, https:\/\/mindthegraph.com\/blog\/wp-content\/uploads\/2023\/02\/crispr-cas9-gene-editing-768x672.jpg 768w, https:\/\/mindthegraph.com\/blog\/wp-content\/uploads\/2023\/02\/crispr-cas9-gene-editing-14x12.jpg 14w, https:\/\/mindthegraph.com\/blog\/wp-content\/uploads\/2023\/02\/crispr-cas9-gene-editing-100x88.jpg 100w, https:\/\/mindthegraph.com\/blog\/wp-content\/uploads\/2023\/02\/crispr-cas9-gene-editing.jpg 1123w\" sizes=\"(max-width: 1024px) 100vw, 1024px\" \/><figcaption class=\"wp-element-caption\"><em>Vyroben\u00e9 s <a href=\"https:\/\/mindthegraph.com\" target=\"_blank\" rel=\"noreferrer noopener\"><strong>Mind the Graph<\/strong><\/a><\/em><\/figcaption><\/figure>\n\n\n\n<div style=\"height:18px\" aria-hidden=\"true\" class=\"wp-block-spacer\"><\/div>\n\n\n\n<h2>Ak\u00e9 s\u00fa obavy z CRISPR?<\/h2>\n\n\n\n<ul>\n<li>Dosta\u0165 CRISPR do buniek je n\u00e1ro\u010dn\u00e9. Vedci objavili techniku, ako to dosiahnu\u0165 pomocou v\u00edrusu, ktor\u00fd bol zmutovan\u00fd tak, aby niesol g\u00e9ny pre vodiacu RNA a Cas9. Ke\u010f\u017ee niektor\u00e9 v\u00edrusy m\u00f4\u017eu infikova\u0165 r\u00f4zne typy buniek, m\u00f4\u017eu nakoniec zmeni\u0165 napr\u00edklad svalov\u00e9 bunky, hoci z\u00e1merom boli pe\u010de\u0148ov\u00e9 bunky.<\/li>\n\n\n\n<li>CRISPR sa pr\u00e1ve testuje na \u013eu\u010foch a vedci sa ob\u00e1vaj\u00fa, ako m\u00f4\u017ee telo a imunitn\u00fd syst\u00e9m reagova\u0165 na v\u00edrusy, ktor\u00e9 obsahuj\u00fa CRISPR, alebo na samotn\u00e9 prvky CRISPR. Ke\u010f\u017ee tieto prvky s\u00fa pre \u010dloveka nezn\u00e1me, imunitn\u00fd syst\u00e9m m\u00f4\u017ee napadn\u00fa\u0165 a zni\u010di\u0165 bunky upraven\u00e9 CRISPR.<\/li>\n\n\n\n<li>CRISPR ob\u010das preru\u0161\u00ed DNA mimo cie\u013eov\u00e9ho g\u00e9nu, \u010do je zn\u00e1me ako \"off-target\" rezanie. Vedci sa ob\u00e1vaj\u00fa, \u017ee tak\u00e9to ne\u00famyseln\u00e9 zmeny m\u00f4\u017eu by\u0165 pr\u00edli\u0161 \u0161kodliv\u00e9 a dokonca rakovinov\u00e9.<\/li>\n\n\n\n<li>\u010eal\u0161\u00edm d\u00f4le\u017eit\u00fdm probl\u00e9mom je, \u017ee modifik\u00e1cia buniek v tele m\u00f4\u017ee ne\u00famyselne zmeni\u0165 spermie alebo vaj\u00ed\u010dka, ktor\u00e9 sa m\u00f4\u017eu prenies\u0165 na bud\u00face gener\u00e1cie.<\/li>\n<\/ul>\n\n\n\n<h3>Etick\u00e9 ot\u00e1zky<\/h3>\n\n\n\n<p>Lie\u010dba CRISPR vyvol\u00e1va aj etick\u00e9 obavy. Niektor\u00e9 z nich s\u00fa uveden\u00e9 ni\u017e\u0161ie:<\/p>\n\n\n\n<ul>\n<li>Ako u\u017e bolo povedan\u00e9, zmena buniek v tele m\u00f4\u017ee omylom ovplyvni\u0165 spermie alebo vaj\u00ed\u010dka, \u010do sa m\u00f4\u017ee prenies\u0165 na bud\u00face gener\u00e1cie. Namiesto lie\u010denia chor\u00f4b sa tieto zmeny m\u00f4\u017eu hypoteticky vyu\u017ei\u0165 na zlep\u0161enie \u017eiaducich vlastnost\u00ed.&nbsp;<\/li>\n\n\n\n<li>Mnoh\u00ed \u013eudia s\u00fa z mor\u00e1lneho a n\u00e1bo\u017eensk\u00e9ho h\u013eadiska proti pou\u017e\u00edvaniu \u013eudsk\u00fdch embry\u00ed vo v\u00fdskume. Vo v\u0161eobecnosti sa v\u00fdskum embry\u00ed m\u00f4\u017ee t\u00fdka\u0165 \u017eivotaschopn\u00fdch alebo ne\u017eivotaschopn\u00fdch embry\u00ed, ktor\u00e9 zostali po IVF, alebo embry\u00ed vytvoren\u00fdch \u0161peci\u00e1lne na \u00fa\u010dely \u0161t\u00fadie. Ka\u017ed\u00fd pr\u00edpad m\u00e1 svoj jedine\u010dn\u00fd s\u00fabor etick\u00fdch probl\u00e9mov.<\/li>\n\n\n\n<li>Existuj\u00fa obavy, \u017ee edit\u00e1cia gen\u00f3mu bude obmedzen\u00e1 na bohat\u00fdch, \u010do preh\u013abi existuj\u00face rozdiely v pr\u00edstupe k zdravotnej starostlivosti, ako aj k in\u00fdm lie\u010debn\u00fdm postupom.<\/li>\n<\/ul>\n\n\n\n<h2>Nestr\u00e1cajte \u010das! Platforma je \u013eahko pou\u017eite\u013en\u00e1 a m\u00f4\u017ee ju pou\u017e\u00edva\u0165 takmer ka\u017ed\u00fd.<\/h2>\n\n\n\n<p>Pomocou \u013eahko pou\u017eite\u013en\u00e9ho n\u00e1stroja m\u00f4\u017eete vytv\u00e1ra\u0165 \u00fa\u017easn\u00e9 infografiky, ilustr\u00e1cie alebo dokonca transformova\u0165 svoju pr\u00e1cu na n\u00e1dhern\u00fd a zrozumite\u013en\u00fd plag\u00e1t. <a href=\"https:\/\/mindthegraph.com\" target=\"_blank\" rel=\"noreferrer noopener\">Pozor na graf<\/a> je pre v\u00e1s vhodn\u00fdm n\u00e1strojom; m\u00f4\u017eete pou\u017ei\u0165 \u0161abl\u00f3ny alebo si dokonca vy\u017eiada\u0165 tak\u00fa, ktor\u00e1 zodpoved\u00e1 va\u0161ej \u00falohe presne pod\u013ea va\u0161ich predst\u00e1v!<\/p>\n\n\n\n<div style=\"height:18px\" aria-hidden=\"true\" class=\"wp-block-spacer\"><\/div>\n\n\n<div class=\"wp-block-image\">\n<figure class=\"aligncenter size-full\"><img decoding=\"async\" loading=\"lazy\" width=\"600\" height=\"338\" src=\"https:\/\/mindthegraph.com\/blog\/wp-content\/uploads\/2022\/10\/r3qiu0qenda-3.gif\" alt=\"\" class=\"wp-image-25130\"\/><\/figure><\/div>\n\n\n<div style=\"height:18px\" aria-hidden=\"true\" class=\"wp-block-spacer\"><\/div>\n\n\n\n<div class=\"is-layout-flex wp-block-buttons\">\n<div class=\"wp-block-button aligncenter\"><a class=\"wp-block-button__link has-background wp-element-button\" href=\"https:\/\/mindthegraph.com\/\" style=\"border-radius:50px;background-color:#dc1866\" target=\"_blank\" rel=\"noreferrer noopener\">Zv\u00fd\u0161te svoj v\u00fdskum pomocou ilustr\u00e1ci\u00ed<\/a><\/div>\n<\/div>\n\n\n\n<div style=\"height:44px\" aria-hidden=\"true\" class=\"wp-block-spacer\"><\/div>\n\n\n\n<div style=\"height:25px\" aria-hidden=\"true\" class=\"wp-block-spacer\"><\/div>\n\n\n\n<p><\/p>","protected":false},"excerpt":{"rendered":"<p>Pochopte, \u010do je CRISPR a ako sa t\u00e1to g\u00e9nov\u00e1 terapia m\u00f4\u017ee pou\u017ei\u0165 na modifik\u00e1ciu DNA, \u010d\u00edm sa zlep\u0161\u00ed lie\u010dba rakoviny.<\/p>","protected":false},"author":28,"featured_media":26609,"comment_status":"closed","ping_status":"closed","sticky":false,"template":"","format":"standard","meta":[],"categories":[959,28],"tags":[],"yoast_head":"<!-- This site is optimized with the Yoast SEO plugin v19.9 - https:\/\/yoast.com\/wordpress\/plugins\/seo\/ -->\n<title>How Does CRISPR Therapy Operate in Gene Therapy?<\/title>\n<meta name=\"description\" content=\"Understand what CRISPR is and how this gene therapy can be used to modify DNA, enhancing the treatment of cancer.\" \/>\n<meta name=\"robots\" content=\"index, follow, max-snippet:-1, max-image-preview:large, max-video-preview:-1\" \/>\n<link rel=\"canonical\" href=\"https:\/\/mindthegraph.com\/blog\/sk\/crispr-terapia\/\" \/>\n<meta property=\"og:locale\" content=\"sk_SK\" \/>\n<meta property=\"og:type\" content=\"article\" \/>\n<meta property=\"og:title\" content=\"How Does CRISPR Therapy Operate in Gene 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